Fitusiran, an investigational siRNA therapeutic targeting antithrombin for the treatment of hemophilia, has shown its efficacy in late-stage trials.
Positive Phase III results from two trials are to be presented on fitusiran at the upcoming American Society of Hematology (ASH) meeting.
Development of the drug has been far from plain sailing.
In 2017, clinical studies with fitusiran were placed on hold following reports of a fatal thrombotic event in…
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Chairman, Sanofi Aventis UK